普通外文研报
US Biopharmaceuticals: EHA 2026 Abstract Planner: AGIO sNDA/confirmatory, BEAM, CRBU
研报英文原文证据摘录
US Biopharmaceuticals: EHA 2026 Abstract Planner: AGIO sNDA/confirmatory, BEAM, CRBU
Abstract Planner
Exhibit 1: EHA 2026 abstract planner
We highlight key presentations for companies across our coverage including BEAM, AGIO, and CRBU
Time
Company Program Type of Data (CEST) Type Abstract No. Titles Importance
June 11th
(Thursday)
BEAM SCD meta-analysis N/A Publication PB4134 Correlation Between Fetal Hemoglobin and Clinical LOW
Outcomes in Sickle Cell Disease: A Model-Based
Meta-Analysis
AGIO mitapivat Clinical N/A Publication PB4160 ENERGIZEKIDS: Mitapivat in Pediatric Patients With MODERATE
Non-Transfusion-Dependent Alpha- or
Beta-Thalassemia
AGIO mitapivat Clinical N/A Publication PB4162 ENERGIZEKIDS-T: Mitapivat in Pediatric Patients MODERATE
With Transfusion-Dependent Alpha- or
AGIO SCD / thalassemia / PKD PRO N/A Publication PB4417 The Patient Experience of Fatigue in Individuals LOW
With Sickle Cell Disease, Thalassemia, and Pyruvate
Kinase Deficiency
AGIO mitapivat Clinical 4:45 - 6:00 Oral S304 Effects of Mitapivat on Iron Burden and Spleen Size MODERATE
PM in Erythrocyte Membranopathies and Congenital
Dyserythropoietic Anemia Type II: 56-Week
Follow-Up Results From the SATISFY Study
June 12th
(Friday)
CRBU vispa-cel Clinical 5:15 - 6:30 Oral S236 Vispa-cel, an allogeneic anti-CD19 CAR-T cell therapy HIGH
PM with a PD-1 knockout, in patients with
relapsed/refractory B cell non-Hodgkin lymphoma
(ANTLER phase 1 clinical trial)
AGIO SCD TBD 6:45 - 7:45 Poster PF1264 Metabolic Profiles Associated With Point of Sickling LOW
PM Reflect Immunoregulation, Oxidative Stress, and
Compensatory Mechanisms in Patients With Sickle
Cell Anemia
AGIO SCD TBD 6:45 - 7:45 Poster PF1269 Impaired Function of Pyruvate Kinase Is Associated MODERATE
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